A gene therapy for patients with X-linked severe combined immunodeficiency (X-SCID) has passed pre-clinical safety and efficacy tests in China – paving the way for trials in the country. Professor Adrian Thrasher from UCL Great Ormond Street Insti...
16 days ago
The first treatment for an inherited immune system disorder first identified in 2013 will be made available to patients in England, it has been announced. Leniolisib will be available for patients over the age of 12 with activated phosphoinositide...
16 days ago